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NA遺伝子治療市場 - 産業動向と2030年までの予測


NA Gene Therapy Market - Industry Trends and Forecast to 2030

北米の遺伝子治療市場は、2023年から2030年にかけて18.3%のCAGRを記録すると予測されています。この新しい市場レポートは、歴史的な年2021年のデータを含み、計算の基準年は2022年で、予測期間は2023年から2030年... もっと見る

 

 

出版社 出版年月 電子版価格 ページ数 言語
Data Bridge Market Research
データブリッジマーケットリサーチ
2023年1月3日 US$3,500
シングルユーザライセンス
ライセンス・価格情報・注文方法はこちら
133 英語

 

サマリー

北米の遺伝子治療市場は、2023年から2030年にかけて18.3%のCAGRを記録すると予測されています。この新しい市場レポートは、歴史的な年2021年のデータを含み、計算の基準年は2022年で、予測期間は2023年から2030年です。
市場セグメンテーションを行います:
北米の遺伝子治療市場、ベクタータイプ別(ウイルスベクター、非ウイルスベクター)、方法別(生体外、生体内)、用途別(腫瘍疾患、心血管疾患、感染症、希少疾患、神経疾患、その他の疾患)、エンドユーザー別(がん研究機関、病院、研究機関、その他)、国(米国、カナダ、メキシコ)産業動向と2030年予測
遺伝子治療市場の成長に寄与する主な要因として、以下のものが挙げられます:

- 個別化医療の需要の高まり
- 遺伝性疾患の有病率の上昇
- 遺伝子治療の新たなアプローチ
市場のプレーヤー:

北米の遺伝子治療市場の主要な市場関係者は以下の通りです:
- AGCバイオロジックス
- アムジェン,Inc.
- アンジェス、インコーポレイテッド
- バイオジェン
- ブルーバード・バイオ・インク
- ブリストル・マイヤーズ スクイブ・カンパニー
- CHIESI Farmaceutici S.p.A.
- デンドレオン・ファーマシューティカルズLLC
- Enzyvant Therapeutics GmbH
- フェリングB.V.
- ヤンセン・ファーマシューティカルズ・インク(Janssen Pharmaceuticals, Inc.
- カイトファーマ(ギリアド・サイエンシズ・インクの子会社)
- マリンクロッド
- ノバルティスAG
- オーチャード・セラピューティクス・ピーエルシー
- オックスフォード・バイオメディカ
- スパーク・セラピューティクス社(Spark Therapeutics, Inc.
- ユニキュアNV.




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目次

TABLE OF CONTENTS
1 INTRODUCTION 20
1.1 OBJECTIVES OF THE STUDY 20
1.2 MARKET DEFINITION 20
1.3 OVERVIEW OF THE NORTH AMERICA GENE THERAPY MARKET 20
1.4 CURRENCY AND PRICING 22
1.5 LIMITATIONS 22
1.6 MARKETS COVERED 22
2 MARKET SEGMENTATION 24
2.1 MARKETS COVERED 24
2.2 GEOGRAPHICAL SCOPE 25
2.3 YEARS CONSIDERED FOR THE STUDY 26
2.4 DBMR TRIPOD DATA VALIDATION MODEL 27
2.5 PRIMARY INTERVIEWS WITH KEY OPINION LEADERS 30
2.6 MULTIVARIATE MODELLING 31
2.7 MARKET END USER COVERAGE GRID 31
2.8 PRODUCT LIFELINE CURVE 32
2.9 DBMR MARKET POSITION GRID 33
2.10 VENDOR SHARE ANALYSIS 34
2.11 SECONDARY SOURCES 35
2.12 ASSUMPTIONS 35
3 EXECUTIVE SUMMARY 36
4 PREMIUM INSIGHTS 39
4.1 PESTEL ANALYSIS 40
4.2 PORTER FIVE ANALYSIS 41
5 UPDATE ON GERMLINE GENE THERAPY 42
5.1 GERMLINE GENE THERAPY 42
6 NORTH AMERICA GENE THERAPY MARKET, MO 43
6.1 DRIVERS 45
6.1.1 NOVEL APPROACHES TO GENE THERAPY 45
6.1.2 INCREASING PREVALENCE OF GENETIC DISORDERS 45
6.1.3 THE GROWING INVESTMENT BY BIOTECHNOLOGY & PHARMACEUTICAL COMPANIES 46
6.1.4 GROWING DEMAND FOR PERSONALIZED MEDICINE 47
6.2 RESTRAINTS 47
6.2.1 HIGH COST OF GENE THERAPY 47
6.2.2 ETHICAL AND SAFETY CONCERNS 48
6.2.3 COMPLEXITY OF GENE THERAPY 48
6.3 OPPORTUNITIES 49
6.3.1 RISE IN STRATEGIC ACQUISITION AND PARTNERSHIP AMONG ORGANIZATIONS 49
6.3.2 RISING APPROVAL FOR GENE THERAPY PRODUCTS 49
6.4 CHALLENGES 50
6.4.1 STRINGENT REGULATIONS FOR GENE THERAPY PRODUCTS 50
6.4.2 LONG-TERM SAFETY AND EFFICACY 50
7 NORTH AMERICA GENE THERAPY MARKET, BY VECTOR TYPE 51
7.1 OVERVIEW 52
7.2 VIRAL VECTOR 55
7.2.1 ADENOVIRUS 56
7.2.2 RETROVIRUS 56
7.2.3 LENTIVIRUS 56
7.2.4 ADENO-ASSOCIATED VIRUS 56
7.2.5 VACCINIA VIRUS 56
7.2.6 HERPES SIMPLEX VIRUS 56
7.2.7 OTHERS 56
7.3 NON-VIRAL VECTOR 56
7.3.1 LIPOFECTION 57
7.3.2 INJECTION OF NAKED DNA 57
8 NORTH AMERICA GENE THERAPY MARKET, BY METHOD 58
8.1 OVERVIEW 59
8.2 EX-VIVO 62
8.3 IN-VIVO 62
9 NORTH AMERICA GENE THERAPY MARKET, BY APPLICATION 64
9.1 OVERVIEW 65
9.2 ONCOLOGICAL DISORDERS 68
9.3 CARDIOVASCULAR DISEASES 68
9.4 INFECTIOUS DISEASES 69
9.5 RARE DISEASES 70
9.6 NUEROLOGICAL DISORDERS 71
9.7 OTHER DISEASES 72
10 NORTH AMERICA GENE THERAPY MARKET, BY END USER 73
10.1 OVERVIEW 74
10.2 CANCER INSTITUTES 77
10.3 HOSPITALS 77
10.4 RESEARCH INSTITUTES 78
10.5 OTHERS 79
11 NORTH AMERICA GENE THERAPY MARKET, BY REGION 80
11.1 NORTH AMERICA 81
11.1.1 U.S. 87
11.1.2 CANADA 89
11.1.3 MEXICO 91
12 NORTH AMERICA GENE THERAPY MARKET, COMPANY LANDSCAPE 93
12.1 COMPANY SHARE ANALYSIS: NORTH AMERICA 93
13 COMPANY PROFILES 94
13.1 BIOGEN 94
13.1.1 COMPANY SNAPSHOT 94
13.1.2 REVENUE ANALYSIS 94
13.1.3 COMPANY SHARE ANALYSIS 95
13.1.4 SWOT ANALYSIS 95
13.1.5 PRODUCT PORTFOLIO 96
13.1.6 RECENT DEVELOPMENT 96
13.2 KITE PHARMA 97
13.2.1 COMPANY SNAPSHOT 97
13.2.2 REVENUE ANALYSIS 97
13.2.3 COMPANY SHARE ANALYSIS 98
13.2.4 SWOT ANALYSIS 98
13.2.5 PRODUCT PORTFOLIO 99
13.2.6 RECENT DEVELOPMENT 99
13.3 NOVARTIS AG 100
13.3.1 COMPANY SNAPSHOT 100
13.3.2 REVENUE ANALYSIS 100
13.3.3 COMPANY SHARE ANALYSIS 101
13.3.4 SWOT ANALYSIS 101
13.3.5 PRODUCT PORTFOLIO 102
13.3.6 RECENT DEVELOPMENTS 102
13.4 BRISTOL-MYERS SQUIBB COMPANY. 103
13.4.1 COMPANY SNAPSHOT 103
13.4.2 REVENUE ANALYSIS 103
13.4.3 COMPANY SHARE ANALYSIS 104
13.4.4 SWOT ANALYSIS 104
13.4.5 PRODUCT PORTFOLIO 105
13.4.6 RECENT DEVELOPMENT 105
13.5 OXFORD BIOMEDICA 106
13.5.1 COMPANY SNAPSHOT 106
13.5.2 REVENUE ANALYSIS 106
13.5.3 COMPANY SHARE ANALYSIS 107
13.5.4 SWOT ANALYSIS 107
13.5.5 PRODUCT PORTFOLIO 108
13.5.6 RECENT DEVELOPMENTS 108
13.6 AGC BIOLOGICS 109
13.6.1 COMPANY SNAPSHOT 109
13.6.2 PRODUCT PORTFOLIO 109
13.6.3 RECENT DEVELOPMENT 109
13.7 ANGES, INC 110
13.7.1 COMPANY SNAPSHOT 110
13.7.2 REVENUE ANALYSIS 110
13.7.3 PRODUCT PORTFOLIO 111
13.7.4 RECENT DEVELOPMENT 111
13.8 AMGEN INC. 112
13.8.1 COMPANY SNAPSHOT 112
13.8.2 REVENUE ANALYSIS 112
13.8.3 PRODUCT PORTFOLIO 113
13.8.4 RECENT DEVELOPMENT 113
13.9 BLUEBIRD BIO, INC. 114
13.9.1 COMPANY SNAPSHOT 114
13.9.2 PRODUCT PORTFOLIO 114
13.9.3 RECENT DEVELOPMENT 114
13.10 CHIESI FARMACEUTICI S.P.A 115
13.10.1 COMPANY SNAPSHOT 115
13.10.2 REVENUE ANALYSIS 115
13.10.3 PRODUCT PORTFOLIO 116
13.10.4 RECENT DEVELOPMENT 116
13.11 DENDREON PHARMACEUTICALS LLC 117
13.11.1 COMPANY SNAPSHOT 117
13.11.2 PRODUCT PORTFOLIO 117
13.11.3 RECENT DEVELOPMENT 117
13.12 ENZYVANT THERAPEUTICS GMBH 118
13.12.1 COMPANY SNAPSHOT 118
13.12.2 RODUCT PORTFOLIO 118
13.12.3 RECENT DEVELOPMENT 118
13.13 FERRING B.V. 119
13.13.1 COMPANY SNAPSHOT 119
13.13.2 PRODUCT PORTFOLIO 119
13.13.3 RECENT DEVELOPMENT 119
13.14 JANSSEN PHARMACEUTICALS, INC. 120
13.14.1 COMPANY SNAPSHOT 120
13.14.2 PRODUCT PORTFOLIO 120
13.14.3 RECENT DEVELOPMENT 120
13.15 MALLINCKRODT. 121
13.15.1 COMPANY SNAPSHOT 121
13.15.2 REVENUE ANALYSIS 121
13.15.3 PRODUCT PORTFOLIO 122
13.15.4 RECENT DEVELOPMENT 122
13.16 ORCHARD THERAPEUTICS PLC. 123
13.16.1 COMPANY SNAPSHOT 123
13.16.2 REVENUE ANALYSIS 123
13.16.3 PRODUCT PORTFOLIO 124
13.16.4 RECENT DEVELOPMENT 124
13.17 SHANGHAI SUNWAY BIOTECH CO., LTD. 125
13.17.1 COMPANY SNAPSHOT 125
13.17.2 PRODUCT PORTFOLIO 125
13.17.3 RECENT DEVELOPMENT 125
13.18 SIBONO 126
13.18.1 COMPANY SNAPSHOT 126
13.18.2 PRODUCT PORTFOLIO 126
13.18.3 RECENT DEVELOPMENT 126
13.19 SPARK THERAPEUTICS, INC. 127
13.19.1 COMPANY SNAPSHOT 127
13.19.2 PRODUCT PORTFOLIO 127
13.19.3 RECENT DEVELOPMENT 127
13.20 UNIQURE NV. 128
13.20.1 COMPANY SNAPSHOT 128
13.20.2 REVENUE ANALYSIS 128
13.20.3 PRODUCT PORTFOLIO 129
13.20.4 RECENT DEVELOPMENT 129
14 QUESTIONNAIRE 130
15 RELATED REPORTS 133

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図表リスト

LIST OF TABLES
TABLE 1 NORTH AMERICA GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 47
TABLE 2 NORTH AMERICA VIRAL VECTOR IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 48
TABLE 3 NORTH AMERICA VIRAL VECTOR IN GENE THERAPY MARKET, BY TYPE, 2021-2030 (USD MILLION) 48
TABLE 4 NORTH AMERICA NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 50
TABLE 5 NORTH AMERICA NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY TYPE, 2021-2030 (USD MILLION) 50
TABLE 6 NORTH AMERICA GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 54
TABLE 7 NORTH AMERICA EX-VIVO IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 55
TABLE 8 NORTH AMERICA IN –VIVO IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 56
TABLE 9 NORTH AMERICA GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 60
TABLE 10 NORTH AMERICA ONCOLOGICAL DISORDERS IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 61
TABLE 11 NORTH AMERICA CARDIOVASCULAR DISEASES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 62
TABLE 12 NORTH AMERICA INFECTIOUS DISEASES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 63
TABLE 13 NORTH AMERICA RARE DISEASES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 64
TABLE 14 NORTH AMERICA NEUROLOGICAL DISORDERS IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 65
TABLE 15 NORTH AMERICA OTHER DISEASES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 65
TABLE 16 NORTH AMERICA GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 69
TABLE 17 NORTH AMERICA CANCER INSTITUTES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 70
TABLE 18 NORTH AMERICA HOSPITALS IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 71
TABLE 19 NORTH AMERICA RESEARCH INSTITUTES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 71
TABLE 20 NORTH AMERICA OTHERS IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 72
TABLE 21 NORTH AMERICA GENE THERAPY MARKET, BY COUNTRY, 2021-2030 (USD MILLION) 78
TABLE 22 NORTH AMERICA GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 78
TABLE 23 NORTH AMERICA VIRAL VECTOR IN GENE THERAPY MARKET, BY TYPE, 2021-2030 (USD MILLION) 78
TABLE 24 NORTH AMERICA NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY TYPE, 2021-2030 (USD MILLION) 78
TABLE 25 NORTH AMERICA GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 78
TABLE 26 NORTH AMERICA GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 79
TABLE 27 NORTH AMERICA GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 79
TABLE 28 U.S. GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 80
TABLE 29 U.S. VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 80
TABLE 30 U.S. NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 80
TABLE 31 U.S. GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 80
TABLE 32 U.S. GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 81
TABLE 33 U.S. GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 81
TABLE 34 CANADA GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 82
TABLE 35 CANADA VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 82
TABLE 36 CANADA NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 82
TABLE 37 CANADA GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 82
TABLE 38 CANADA GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 83
TABLE 39 CANADA GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 83
TABLE 40 MEXICO GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 84
TABLE 41 MEXICO VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 84
TABLE 42 MEXICO NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 84
TABLE 43 MEXICO GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 84
TABLE 44 MEXICO GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 85
TABLE 45 MEXICO GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 85

 

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Summary

North America gene therapy market is projected to register a CAGR of 18.3% from 2023 to 2030. The new market report contains data for the historic year 2021, the base year of calculation is 2022, and the forecast period is 2023 to 2030.
Market Segmentation:
North America Gene Therapy Market, By Vector Type (Viral Vector and Non-viral Vector), Method (Ex-vivo and In-vivo), Application (Oncological Disorders, Cardiovascular Diseases, Infectious Diseases, Rare Diseases, Neurological Disorders, and Other Diseases), End User (Cancer Institutes, Hospitals, Research institutes, and Others), Country (U.S., Canada, and Mexico) Industry Trends and Forecast to 2030
Some of the major factors contributing to the growth of the gene therapy market are:

• Rising demand of personalized medicine
• Rising prevalence of genetic disorders
• Novel approaches of gene therapy
Market Players:

The key market players for North America gene therapy market are listed below:
• AGC Biologics
• Amgen,Inc.
• AnGes, Inc
• Biogen
• bluebird bio, Inc.
• Bristol Myers Squibb Company
• CHIESI Farmaceutici S.p.A.
• Dendreon Pharmaceuticals LLC
• Enzyvant Therapeutics GmbH
• Ferring B.V.
• Janssen Pharmaceuticals, Inc.
• Kite Pharma (a subsidiary of Gilead Sciences, Inc.)
• Mallinckrodt.
• Novartis AG
• Orchard Therapeutics plc.
• Oxford Biomedica
• Spark Therapeutics, Inc.
• uniQure NV.




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Table of Contents

TABLE OF CONTENTS
1 INTRODUCTION 20
1.1 OBJECTIVES OF THE STUDY 20
1.2 MARKET DEFINITION 20
1.3 OVERVIEW OF THE NORTH AMERICA GENE THERAPY MARKET 20
1.4 CURRENCY AND PRICING 22
1.5 LIMITATIONS 22
1.6 MARKETS COVERED 22
2 MARKET SEGMENTATION 24
2.1 MARKETS COVERED 24
2.2 GEOGRAPHICAL SCOPE 25
2.3 YEARS CONSIDERED FOR THE STUDY 26
2.4 DBMR TRIPOD DATA VALIDATION MODEL 27
2.5 PRIMARY INTERVIEWS WITH KEY OPINION LEADERS 30
2.6 MULTIVARIATE MODELLING 31
2.7 MARKET END USER COVERAGE GRID 31
2.8 PRODUCT LIFELINE CURVE 32
2.9 DBMR MARKET POSITION GRID 33
2.10 VENDOR SHARE ANALYSIS 34
2.11 SECONDARY SOURCES 35
2.12 ASSUMPTIONS 35
3 EXECUTIVE SUMMARY 36
4 PREMIUM INSIGHTS 39
4.1 PESTEL ANALYSIS 40
4.2 PORTER FIVE ANALYSIS 41
5 UPDATE ON GERMLINE GENE THERAPY 42
5.1 GERMLINE GENE THERAPY 42
6 NORTH AMERICA GENE THERAPY MARKET, MO 43
6.1 DRIVERS 45
6.1.1 NOVEL APPROACHES TO GENE THERAPY 45
6.1.2 INCREASING PREVALENCE OF GENETIC DISORDERS 45
6.1.3 THE GROWING INVESTMENT BY BIOTECHNOLOGY & PHARMACEUTICAL COMPANIES 46
6.1.4 GROWING DEMAND FOR PERSONALIZED MEDICINE 47
6.2 RESTRAINTS 47
6.2.1 HIGH COST OF GENE THERAPY 47
6.2.2 ETHICAL AND SAFETY CONCERNS 48
6.2.3 COMPLEXITY OF GENE THERAPY 48
6.3 OPPORTUNITIES 49
6.3.1 RISE IN STRATEGIC ACQUISITION AND PARTNERSHIP AMONG ORGANIZATIONS 49
6.3.2 RISING APPROVAL FOR GENE THERAPY PRODUCTS 49
6.4 CHALLENGES 50
6.4.1 STRINGENT REGULATIONS FOR GENE THERAPY PRODUCTS 50
6.4.2 LONG-TERM SAFETY AND EFFICACY 50
7 NORTH AMERICA GENE THERAPY MARKET, BY VECTOR TYPE 51
7.1 OVERVIEW 52
7.2 VIRAL VECTOR 55
7.2.1 ADENOVIRUS 56
7.2.2 RETROVIRUS 56
7.2.3 LENTIVIRUS 56
7.2.4 ADENO-ASSOCIATED VIRUS 56
7.2.5 VACCINIA VIRUS 56
7.2.6 HERPES SIMPLEX VIRUS 56
7.2.7 OTHERS 56
7.3 NON-VIRAL VECTOR 56
7.3.1 LIPOFECTION 57
7.3.2 INJECTION OF NAKED DNA 57
8 NORTH AMERICA GENE THERAPY MARKET, BY METHOD 58
8.1 OVERVIEW 59
8.2 EX-VIVO 62
8.3 IN-VIVO 62
9 NORTH AMERICA GENE THERAPY MARKET, BY APPLICATION 64
9.1 OVERVIEW 65
9.2 ONCOLOGICAL DISORDERS 68
9.3 CARDIOVASCULAR DISEASES 68
9.4 INFECTIOUS DISEASES 69
9.5 RARE DISEASES 70
9.6 NUEROLOGICAL DISORDERS 71
9.7 OTHER DISEASES 72
10 NORTH AMERICA GENE THERAPY MARKET, BY END USER 73
10.1 OVERVIEW 74
10.2 CANCER INSTITUTES 77
10.3 HOSPITALS 77
10.4 RESEARCH INSTITUTES 78
10.5 OTHERS 79
11 NORTH AMERICA GENE THERAPY MARKET, BY REGION 80
11.1 NORTH AMERICA 81
11.1.1 U.S. 87
11.1.2 CANADA 89
11.1.3 MEXICO 91
12 NORTH AMERICA GENE THERAPY MARKET, COMPANY LANDSCAPE 93
12.1 COMPANY SHARE ANALYSIS: NORTH AMERICA 93
13 COMPANY PROFILES 94
13.1 BIOGEN 94
13.1.1 COMPANY SNAPSHOT 94
13.1.2 REVENUE ANALYSIS 94
13.1.3 COMPANY SHARE ANALYSIS 95
13.1.4 SWOT ANALYSIS 95
13.1.5 PRODUCT PORTFOLIO 96
13.1.6 RECENT DEVELOPMENT 96
13.2 KITE PHARMA 97
13.2.1 COMPANY SNAPSHOT 97
13.2.2 REVENUE ANALYSIS 97
13.2.3 COMPANY SHARE ANALYSIS 98
13.2.4 SWOT ANALYSIS 98
13.2.5 PRODUCT PORTFOLIO 99
13.2.6 RECENT DEVELOPMENT 99
13.3 NOVARTIS AG 100
13.3.1 COMPANY SNAPSHOT 100
13.3.2 REVENUE ANALYSIS 100
13.3.3 COMPANY SHARE ANALYSIS 101
13.3.4 SWOT ANALYSIS 101
13.3.5 PRODUCT PORTFOLIO 102
13.3.6 RECENT DEVELOPMENTS 102
13.4 BRISTOL-MYERS SQUIBB COMPANY. 103
13.4.1 COMPANY SNAPSHOT 103
13.4.2 REVENUE ANALYSIS 103
13.4.3 COMPANY SHARE ANALYSIS 104
13.4.4 SWOT ANALYSIS 104
13.4.5 PRODUCT PORTFOLIO 105
13.4.6 RECENT DEVELOPMENT 105
13.5 OXFORD BIOMEDICA 106
13.5.1 COMPANY SNAPSHOT 106
13.5.2 REVENUE ANALYSIS 106
13.5.3 COMPANY SHARE ANALYSIS 107
13.5.4 SWOT ANALYSIS 107
13.5.5 PRODUCT PORTFOLIO 108
13.5.6 RECENT DEVELOPMENTS 108
13.6 AGC BIOLOGICS 109
13.6.1 COMPANY SNAPSHOT 109
13.6.2 PRODUCT PORTFOLIO 109
13.6.3 RECENT DEVELOPMENT 109
13.7 ANGES, INC 110
13.7.1 COMPANY SNAPSHOT 110
13.7.2 REVENUE ANALYSIS 110
13.7.3 PRODUCT PORTFOLIO 111
13.7.4 RECENT DEVELOPMENT 111
13.8 AMGEN INC. 112
13.8.1 COMPANY SNAPSHOT 112
13.8.2 REVENUE ANALYSIS 112
13.8.3 PRODUCT PORTFOLIO 113
13.8.4 RECENT DEVELOPMENT 113
13.9 BLUEBIRD BIO, INC. 114
13.9.1 COMPANY SNAPSHOT 114
13.9.2 PRODUCT PORTFOLIO 114
13.9.3 RECENT DEVELOPMENT 114
13.10 CHIESI FARMACEUTICI S.P.A 115
13.10.1 COMPANY SNAPSHOT 115
13.10.2 REVENUE ANALYSIS 115
13.10.3 PRODUCT PORTFOLIO 116
13.10.4 RECENT DEVELOPMENT 116
13.11 DENDREON PHARMACEUTICALS LLC 117
13.11.1 COMPANY SNAPSHOT 117
13.11.2 PRODUCT PORTFOLIO 117
13.11.3 RECENT DEVELOPMENT 117
13.12 ENZYVANT THERAPEUTICS GMBH 118
13.12.1 COMPANY SNAPSHOT 118
13.12.2 RODUCT PORTFOLIO 118
13.12.3 RECENT DEVELOPMENT 118
13.13 FERRING B.V. 119
13.13.1 COMPANY SNAPSHOT 119
13.13.2 PRODUCT PORTFOLIO 119
13.13.3 RECENT DEVELOPMENT 119
13.14 JANSSEN PHARMACEUTICALS, INC. 120
13.14.1 COMPANY SNAPSHOT 120
13.14.2 PRODUCT PORTFOLIO 120
13.14.3 RECENT DEVELOPMENT 120
13.15 MALLINCKRODT. 121
13.15.1 COMPANY SNAPSHOT 121
13.15.2 REVENUE ANALYSIS 121
13.15.3 PRODUCT PORTFOLIO 122
13.15.4 RECENT DEVELOPMENT 122
13.16 ORCHARD THERAPEUTICS PLC. 123
13.16.1 COMPANY SNAPSHOT 123
13.16.2 REVENUE ANALYSIS 123
13.16.3 PRODUCT PORTFOLIO 124
13.16.4 RECENT DEVELOPMENT 124
13.17 SHANGHAI SUNWAY BIOTECH CO., LTD. 125
13.17.1 COMPANY SNAPSHOT 125
13.17.2 PRODUCT PORTFOLIO 125
13.17.3 RECENT DEVELOPMENT 125
13.18 SIBONO 126
13.18.1 COMPANY SNAPSHOT 126
13.18.2 PRODUCT PORTFOLIO 126
13.18.3 RECENT DEVELOPMENT 126
13.19 SPARK THERAPEUTICS, INC. 127
13.19.1 COMPANY SNAPSHOT 127
13.19.2 PRODUCT PORTFOLIO 127
13.19.3 RECENT DEVELOPMENT 127
13.20 UNIQURE NV. 128
13.20.1 COMPANY SNAPSHOT 128
13.20.2 REVENUE ANALYSIS 128
13.20.3 PRODUCT PORTFOLIO 129
13.20.4 RECENT DEVELOPMENT 129
14 QUESTIONNAIRE 130
15 RELATED REPORTS 133

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List of Tables/Graphs

LIST OF TABLES
TABLE 1 NORTH AMERICA GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 47
TABLE 2 NORTH AMERICA VIRAL VECTOR IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 48
TABLE 3 NORTH AMERICA VIRAL VECTOR IN GENE THERAPY MARKET, BY TYPE, 2021-2030 (USD MILLION) 48
TABLE 4 NORTH AMERICA NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 50
TABLE 5 NORTH AMERICA NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY TYPE, 2021-2030 (USD MILLION) 50
TABLE 6 NORTH AMERICA GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 54
TABLE 7 NORTH AMERICA EX-VIVO IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 55
TABLE 8 NORTH AMERICA IN –VIVO IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 56
TABLE 9 NORTH AMERICA GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 60
TABLE 10 NORTH AMERICA ONCOLOGICAL DISORDERS IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 61
TABLE 11 NORTH AMERICA CARDIOVASCULAR DISEASES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 62
TABLE 12 NORTH AMERICA INFECTIOUS DISEASES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 63
TABLE 13 NORTH AMERICA RARE DISEASES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 64
TABLE 14 NORTH AMERICA NEUROLOGICAL DISORDERS IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 65
TABLE 15 NORTH AMERICA OTHER DISEASES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 65
TABLE 16 NORTH AMERICA GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 69
TABLE 17 NORTH AMERICA CANCER INSTITUTES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 70
TABLE 18 NORTH AMERICA HOSPITALS IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 71
TABLE 19 NORTH AMERICA RESEARCH INSTITUTES IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 71
TABLE 20 NORTH AMERICA OTHERS IN GENE THERAPY MARKET, BY REGION, 2021-2030 (USD MILLION) 72
TABLE 21 NORTH AMERICA GENE THERAPY MARKET, BY COUNTRY, 2021-2030 (USD MILLION) 78
TABLE 22 NORTH AMERICA GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 78
TABLE 23 NORTH AMERICA VIRAL VECTOR IN GENE THERAPY MARKET, BY TYPE, 2021-2030 (USD MILLION) 78
TABLE 24 NORTH AMERICA NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY TYPE, 2021-2030 (USD MILLION) 78
TABLE 25 NORTH AMERICA GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 78
TABLE 26 NORTH AMERICA GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 79
TABLE 27 NORTH AMERICA GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 79
TABLE 28 U.S. GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 80
TABLE 29 U.S. VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 80
TABLE 30 U.S. NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 80
TABLE 31 U.S. GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 80
TABLE 32 U.S. GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 81
TABLE 33 U.S. GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 81
TABLE 34 CANADA GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 82
TABLE 35 CANADA VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 82
TABLE 36 CANADA NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 82
TABLE 37 CANADA GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 82
TABLE 38 CANADA GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 83
TABLE 39 CANADA GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 83
TABLE 40 MEXICO GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 84
TABLE 41 MEXICO VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 84
TABLE 42 MEXICO NON-VIRAL VECTOR IN GENE THERAPY MARKET, BY VECTOR TYPE, 2021-2030 (USD MILLION) 84
TABLE 43 MEXICO GENE THERAPY MARKET, BY METHOD, 2021-2030 (USD MILLION) 84
TABLE 44 MEXICO GENE THERAPY MARKET, BY APPLICATION, 2021-2030 (USD MILLION) 85
TABLE 45 MEXICO GENE THERAPY MARKET, BY END USER, 2021-2030 (USD MILLION) 85

 

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